F.D.A. Approves 2 Sickle Cell Treatments, One Using CRISPR Gene Editing
People with the genetic disease have new opportunities to eliminate [...]
New Sickle Cell Therapies Will Be Out of Reach Where They Are Needed Most
There is no clear path for African patients to get [...]
Sickle-Cell Treatment Created With Gene Editing Wins U.K. Approval
The first treatment that relies on CRISPR is expected to [...]
Panel Tells F.D.A. That CRISPR Sickle Cell Cure Is Safe Enough for Patients
The decision by an advisory committee may lead to Food [...]
F.D.A. Experts Will Vote on Safety of a Cure for Sickle Cell Disease
The treatment from the company Vertex would be the first [...]
Suddenly, It Looks Like We’re in a Golden Age for Medicine
We may be on the cusp of an era of [...]
A Dilemma for Governments: How to Pay for Million-Dollar Therapies
A wave of transformative but hugely expensive treatments is challenging [...]
Alzheimer’s APOE4 Genetic Risk Targeted in Promising Trial
Preliminary results offer hope that gene therapy can protect people [...]
Gene Treatment for Rare Epilepsy Causes Brain Side Effect in 2 Children
The side effect, a buildup of fluid in the brain, [...]