FDA Approves Journavx Drug to Treat Pain Without Addiction Risk
The drug, Journavx by Vertex Pharmaceuticals, blocks pain signals to [...]
F.D.A. Approves 2 Sickle Cell Treatments, One Using CRISPR Gene Editing
People with the genetic disease have new opportunities to eliminate [...]
New Sickle Cell Therapies Will Be Out of Reach Where They Are Needed Most
There is no clear path for African patients to get [...]
Sickle-Cell Treatment Created With Gene Editing Wins U.K. Approval
The first treatment that relies on CRISPR is expected to [...]
Panel Tells F.D.A. That CRISPR Sickle Cell Cure Is Safe Enough for Patients
The decision by an advisory committee may lead to Food [...]
F.D.A. Experts Will Vote on Safety of a Cure for Sickle Cell Disease
The treatment from the company Vertex would be the first [...]
‘Miracle’ Cystic Fibrosis Drug Kept Out of Reach in Developing Countries
Vertex Pharmaceuticals is not making its drug, Trikafta, available in [...]
La larga espera por la cura de la diabetes
Un documental recoge la desesperación y la frustración de los [...]
The Long, Long Wait for a Diabetes Cure
A documentary captures the desperation and frustration of Type 1 [...]
A Cure for Type 1 Diabetes? For One Man, It Seems to Have Worked.
A new treatment using stem cells that produce insulin has [...]