F.D.A. Experts Will Vote on Safety of a Cure for Sickle Cell Disease
The treatment from the company Vertex would be the first [...]
Suddenly, It Looks Like We’re in a Golden Age for Medicine
We may be on the cusp of an era of [...]
A Dilemma for Governments: How to Pay for Million-Dollar Therapies
A wave of transformative but hugely expensive treatments is challenging [...]
Alzheimer’s APOE4 Genetic Risk Targeted in Promising Trial
Preliminary results offer hope that gene therapy can protect people [...]
Gene Treatment for Rare Epilepsy Causes Brain Side Effect in 2 Children
The side effect, a buildup of fluid in the brain, [...]